Lights! Camera! Action! Join us for an educational experience that makes the science behind gene therapy research memorable and entertaining. Will you become the next Jeopardy gene-ius?

This session will introduce advocates to market research that was conducted to define the lexicon of gene therapy research to provide a foundation for clear and compelling language to explain the principles behind gene therapy research.

This presentation will outline what’s unique about how investigational gene therapies are shipped, stored, and aministered. Join us to walk through a clinical trial participant’s pre-infusion, infusion day, and immediate post-infusion monitoring.

Follow up and monitoring are key elements of the gene therapy clinical trial experience. We will discuss how those clinical trials address post-infusion follow-up and monitoring to collect safety and efficacy data.

This session will provide an overview of the different approaches being considered for providing access to one-time treatments like cell and gene therapies that are under investigation. We invite you to learn more about potential alternative payment models and policy initiatives that may support treatments that are delivered on a one-time basis.